Latest Drugs, Latest Approval in Miscellaneous metabolic agents

What are Miscellaneous metabolic agents?

Metabolic agents are substances capable of producing an effect on the sum of the chemical and physical changes occurring in tissue, consisting of those reactions that convert small molecules into large (anabolism), and those reactions that convert large molecules into small (catabolism ). Miscellaneous metabolic agents includes all metabolic agents not classified elsewhere.

Name Updated
Opfolda (Miglustat) 29-Sep-2023
Metreleptin (Metreleptin [ met-re-lep-tin ]) 17-Aug-2023
Burosumab (Burosumab [ bur-oh-sue-mab ]) 16-Aug-2023
Mitapivat (Mitapivat [ mye-ta-piv-at ]) 16-Aug-2023
Sapropterin (Sapropterin [ sap-roe-ter-in ]) 15-Aug-2023
Inotersen (Inotersen [ in-oh-ter-sen ]) 14-Aug-2023
Givosiran (Givosiran [ gi-voe-si-ran ]) 14-Aug-2023
Fosdenopterin (Fosdenopterin [ fos-den-op-ter-in ]) 14-Aug-2023
Eliglustat (Eliglustat [ el-i-gloo-stat ]) 14-Aug-2023
Pegvaliase (Pegvaliase [ peg-val-i-ase ]) 14-Aug-2023
Miglustat (Miglustat [ mi-gloo-stat ]) 13-Aug-2023
Migalastat (Migalastat [ mi-gal-a-stat ]) 13-Aug-2023
Lumasiran (Lumasiran [ loo-ma-sir-an ]) 13-Aug-2023
Lonafarnib (Lonafarnib [ loe-na-far-nib ]) 13-Aug-2023
Asfotase alfa (Asfotase alfa [ as-foe-tase-al-fa ]) 13-Aug-2023
Uridine triacetate (Uridine triacetate [ ure-i-deen-trye-as-e-tate ]) 12-Aug-2023
Pyrukynd taper pack (Mitapivat [ mye-ta-piv-at ]) 12-Aug-2023
Pyrukynd (Mitapivat) 12-Aug-2023
Patisiran (Patisiran [ pat-i-sir-an ]) 11-Aug-2023
Nitisinone (Nitisinone [ nye-tis-i-none ]) 11-Aug-2023
Amvuttra (Vutrisiran) 05-Aug-2023
Orfadin (Nitisinone [ nye-tis-i-none ]) 05-Aug-2023
Cerdelga (Eliglustat [ el-i-gloo-stat ]) 05-Aug-2023
Zokinvy (Lonafarnib [ loe-na-far-nib ]) 14-Jul-2023
Zavesca (Miglustat [ mi-gloo-stat ]) 14-Jul-2023
Vistogard (Uridine triacetate [ ure-i-deen-trye-as-e-tate ]) 14-Jul-2023
Tegsedi (Inotersen [ in-oh-ter-sen ]) 14-Jul-2023
Strensiq (Asfotase alfa [ as-foe-tase-al-fa ]) 14-Jul-2023
Palynziq (Pegvaliase [ peg-val-i-ase ]) 13-Jul-2023
Oxlumo (Lumasiran [ loo-ma-sir-an ]) 13-Jul-2023
Nulibry (Fosdenopterin [ fos-den-op-ter-in ]) 13-Jul-2023
Nityr (Nitisinone [ nye-tis-i-none ]) 13-Jul-2023
Myalept (Metreleptin [ met-re-lep-tin ]) 13-Jul-2023
Givlaari (Givosiran [ gi-voe-si-ran ]) 13-Jul-2023
Galafold (Migalastat [ mi-gal-a-stat ]) 13-Jul-2023
Crysvita (Burosumab [ bur-oh-sue-mab ]) 13-Jul-2023
Onpattro (Patisiran [ pat-i-sir-an ]) 11-Jul-2023