Answers by TheMediTary.Com - Last updated: 14-Jul-2023
Exondys 51 is administered once a week as a 35 to 60-minute intravenous infusion by your healthcare provider. The correct dosage of Exondys 51 is drawn up and then diluted in an infusion bag containing 0.9% sodium chloride to make a total volume of 100-150 mL. The diluted solution is then administered into one of your veins via an in-line 0.2-micron filter.
Exondys 51 is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed mutation of the DMD gene that is amenable to exon 51 skipping.