Answers by TheMediTary.Com - Last updated: 14-Jul-2023
Exondys 51 can only be used by patients with DMD who have a confirmed mutation in their dystrophin gene that can be treated by skipping exon 51. This works out to be about 13% of people with DMD.
Ask your doctor about genetic testing and if you haven’t already done so, ask for a genetic test for your child. This test can identify the genetic mutation and if it is amenable to treatment with Exondys 51. Genetic testing methods have changed with time, so ask your doctor to order a new test if the test was done years ago.