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Home > Drugs > Treatments > Pompe disease

Medications for Pompe disease

Glycogen storage disease type II (also called Pompe disease or acid maltase deficiency) is a neuromuscular, autosomal recessive metabolic disorder in the family of lysosomal storage diseases caused by a deficiency in the enzyme Acid alpha-glucosidase (EC 3.2.1.20), which is needed to break down glycogen—a long, branched glucose polymer and stored form of sugar used for energy. It is the only glycogen storage disease with a defect in lysosomal metabolism and was the first glycogen storage disease to be identified, in 1932.

The build-up of glycogen causes progressive muscle weakness (myopathy) throughout the body and affects various body tissues, particularly in the heart, skeletal muscles, liver and nervous system.

The disease is named after Johann Pompe, who characterized it in 1932.

Drugs used to treat Pompe disease

Name Drug Class Updated
Alglucosidase alfa (injection) Lysosomal enzymes 13-Aug-2023
Avalglucosidase alfa Lysosomal enzymes 11-Aug-2023
Nexviazyme Lysosomal enzymes 13-Jul-2023
Myozyme injection Lysosomal enzymes 13-Jul-2023
Lumizyme injection Lysosomal enzymes 13-Jul-2023
Lumizyme injection Lysosomal enzymes 05-Sep-2023
Pombiliti Drugs 29-Sep-2023
Opfolda Miscellaneous metabolic agents 29-Sep-2023
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