Transcobalamin II deficiency is a rare autosomal recessive disease. Transcobalamin II transports vitamin B12, hence the main symptom of the disease is Megaloblastic anemia.
Drugs used to treat Transcobalamin II Deficiency
| Name | Drug Class |
|---|---|
| Hydroxocobalamin (injection) | Vitamins |
| Cyanokit | Vitamins |