Other names: PKU
Phenylketonuria (PKU) is a rare hereditary condition in which the amino acid phenylalanine is not properly metabolized. PKU can cause severe mental retardation if not treated.
Drugs used to treat Phenylketonuria
| Name | Drug Class |
|---|---|
| Sapropterin | Miscellaneous metabolic agents |
| Pegvaliase | Miscellaneous metabolic agents |
| Palynziq | Miscellaneous metabolic agents |
| Javygtor | Drugs |
