Spinal Muscular Atrophy is a hereditary neuromuscular disease affecting motor neurons in the spinal cord, characterized by weakness and progressive muscle wasting. It is caused by a mutation in the survival motor neuron gene 1 (SMN1).
Spinal Muscular Atrophy is a hereditary neuromuscular disease affecting motor neurons in the spinal cord, characterized by weakness and progressive muscle wasting. It is caused by a mutation in the survival motor neuron gene 1 (SMN1).
Name | Drug Class | Updated |
---|---|---|
Risdiplam | Miscellaneous uncategorized agents | 12-Aug-2023 |
Onasemnogene abeparvovec (zolgensma) | Miscellaneous uncategorized agents | 11-Aug-2023 |
Nusinersen (injection) | Miscellaneous uncategorized agents | 11-Aug-2023 |
Zolgensma | Miscellaneous uncategorized agents | 14-Jul-2023 |
Evrysdi | Miscellaneous uncategorized agents | 13-Jul-2023 |
Spinraza | Miscellaneous uncategorized agents | 12-Jul-2023 |